To assess the market opportunity for a novel Hemophilia A therapy in order to facilitate their discussions with national/regional payers across USA and EU5.
To seek input on target product profiles and requisite data of interest and overall opinion on value based agreements.
Unimrkt conducted the assessment in two stages – Stage 1 of desk research and stage 2 of primary research with the target groups.
Desk Research
Unimrkt reviewed clinical guidelines in the USA and EU5 and analyzed the trends in actual clinical practice, primarily where differing from the clinical guidelines
Primary Research
Overall structure, and differentiating factors accounted for Rare disease products
Product and pricing evaluation factors by HTA bodies like NICE, IQWiG, HAS, commercial payers, CMS, etc.
Pricing structure of current standard of care product in the Hemophilia A care
We conducted telephonic interviews with the USA & EU5 countries payers.
Sample size: Total 150 interviews with payers; 30 payers in each of the countries (USA -30, EU5 countries - 120)